Gene therapy prevents death, restores growth in mice and a calf with maple syrup urine disease
A one-time injection of a novel gene therapy was able to save mice and a newborn calf from succumbing to maple syrup urine disease, suggesting the treatment could one day be used to treat patients with the rare genetic disorder.
A one-time injection of a novel gene therapy was able to save mice and a newborn calf from succumbing to maple syrup urine disease, suggesting the treatment could one day be used to treat patients with the rare genetic disorder.
