Rilzabrutinib Granted Orphan Drug Designation in the US for Sickle Cell Disease

Paris, June 3, 2025. The US Food and Drug Administration (FDA) has granted orphan drug designation to rilzabrutinib, a novel, advanced, oral, reversible Bruton's tyrosine kinase (BTK) inhibitor that works via multi-immune modulation, to target a...

Jun 3, 2025 - 22:55
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Rilzabrutinib Granted Orphan Drug Designation in the US for Sickle Cell Disease
Paris, June 3, 2025. The US Food and Drug Administration (FDA) has granted orphan drug designation to rilzabrutinib, a novel, advanced, oral, reversible Bruton's tyrosine kinase (BTK) inhibitor that works via multi-immune modulation, to target a...