Chasing Sarepta, RegenXBio links DMD gene therapy to improved outcomes

RegenXBio has shared updated phase 1/2 data on its Duchenne muscular dystrophy (DMD) gene therapy, providing evidence that its pivotal dose improves functional outcomes in older boys with the disease.

Jun 5, 2025 - 14:55
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Chasing Sarepta, RegenXBio links DMD gene therapy to improved outcomes
RegenXBio has shared updated phase 1/2 data on its Duchenne muscular dystrophy (DMD) gene therapy, providing evidence that its pivotal dose improves functional outcomes in older boys with the disease.