Zevra Therapeutics embarks on diagnosis push as Miplyffa launch gains steam

Niemann-Pick disease type C therapy Miplyffa became commercially available in late November and by the year's end, a total of 109 prescription enrollment forms had been submitted. The company estimates there are around 900 patients with the disease in the U.S.

Mar 13, 2025 - 16:35
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Zevra Therapeutics embarks on diagnosis push as Miplyffa launch gains steam
Niemann-Pick disease type C therapy Miplyffa became commercially available in late November and by the year's end, a total of 109 prescription enrollment forms had been submitted. The company estimates there are around 900 patients with the disease in the U.S.