Orphan designation: (S)-2-amino-6-(2-hydroxypropanoyl)-7,8-dihydropteridin-4(3H)-one Treatment of hyperphenylalaninemia, 20/05/2021 Positive
Orphan designation: (S)-2-amino-6-(2-hydroxypropanoyl)-7,8-dihydropteridin-4(3H)-one Treatment of hyperphenylalaninemia, 20/05/2021 Positive
