Orphan designation: Fragment antibody targeting human TfR1 conjugated to phosphorodiamidate morpholino oligomer Treatment of Duchenne muscular dystrophy, 16/04/2025 Positive
Orphan designation: Fragment antibody targeting human TfR1 conjugated to phosphorodiamidate morpholino oligomer Treatment of Duchenne muscular dystrophy, 16/04/2025 Positive
