Second Duchenne patient dies after receiving Sarepta gene therapy

Another person treated with Elevidys suffered acute liver failure, leading Sarepta to discontinue treatment in certain patients while it evaluates new safety precautions. 

Jun 16, 2025 - 15:00
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Second Duchenne patient dies after receiving Sarepta gene therapy

Another person treated with Elevidys suffered acute liver failure, leading Sarepta to discontinue treatment in certain patients while it evaluates new safety precautions.