AstraZeneca touts early Ultomiris survival data in children living with rare post-transplant complication

In initial results from a phase 3 trial, Ultomiris helped pediatric patients with thrombotic microangiopathy (TMA) after hematopoietic stem cell transplantation (HSCT) achieve an overall survival rate of 87.2% at 26 weeks, AstraZeneca said. The data could help position Ultomiris to help address a potentially deadly post-transplant complication with no targeted treatment options.

Jun 16, 2025 - 16:20
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AstraZeneca touts early Ultomiris survival data in children living with rare post-transplant complication
In initial results from a phase 3 trial, Ultomiris helped pediatric patients with thrombotic microangiopathy (TMA) after hematopoietic stem cell transplantation (HSCT) achieve an overall survival rate of 87.2% at 26 weeks, AstraZeneca said. The data could help position Ultomiris to help address a potentially deadly post-transplant complication with no targeted treatment options.