Orphan designation: Humanised IGg1 monoclonal antibody targeting human transferrin receptor conjugated to human iduronate-2-sulfatase Treatment of mucopolysaccharidosis type II (Hunter's syndrome), 26/02/2019 Positive
Orphan designation: Humanised IGg1 monoclonal antibody targeting human transferrin receptor conjugated to human iduronate-2-sulfatase Treatment of mucopolysaccharidosis type II (Hunter's syndrome), 26/02/2019 Positive
Orphan designation: Humanised IGg1 monoclonal antibody targeting human transferrin receptor conjugated to human iduronate-2-sulfatase Treatment of mucopolysaccharidosis type II (Hunter's syndrome), 26/02/2019 Positive
