Orphan designation: Synthetic oligonucleotide selectively targeting UBE3A antisense RNA transcripts Treatment of Angelman syndrome, 09/12/2020 Positive
Orphan designation: Synthetic oligonucleotide selectively targeting UBE3A antisense RNA transcripts Treatment of Angelman syndrome, 09/12/2020 Positive
Orphan designation: Synthetic oligonucleotide selectively targeting UBE3A antisense RNA transcripts Treatment of Angelman syndrome, 09/12/2020 Positive
